Prion Disease Treatment: Promising Advances in Gene Editing

May 3, 2025

Recent advancements in prion disease treatment are offering hope to patients and researchers alike, particularly as new gene editing therapies emerge to combat these rare and fatal disorders caused by misfolded proteins in the brain.Prion diseases such as Creutzfeldt-Jakob disease and fatal familial insomnia pose serious challenges, but innovative approaches like base editing technology are paving the way for potential breakthroughs.
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